TY  - JOUR

T1  - Translating SOD1 gene silencing towards the clinic: A highly efficacious, off-target free and biomarker-supported strategy for familial ALS

JO  - Molecular Therapy : Nucleic Acids

UR  - https://eprints.whiterose.ac.uk/id/eprint/130343

UR  - https://doi.org/10.1016/j.omtn.2018.04.015

PY  - 2018/09/07

AU  - Iannitti T

AU  - Scarrott J

AU  - Likhite S

AU  - Coldicott IRP

AU  - Lewis KE

AU  - Heath PR

AU  - Higginbottom A

AU  - Myszczynska MA

AU  - Milo M

AU  - Hautbergue GM

AU  - Meyer K et al

ED  - 

DO  - DOI: 10.1016/j.omtn.2018.04.015

PB  - Nature Publishing Group

VL  - 12

SP  - 75

EP  - 88

Y2  - 2025/03/11

ER  -